About PackGene

AAV 製造の革新で、遺伝子治療を「手に取れるもの」「手頃なもの」に

PackGene Biotech は 2014 年、「人生を変える遺伝子治療を、誰もがアクセスしやすいものにする」という共通の想いを持つ、先見の明あるサイエンティストたちによって設立されました。アデノ随伴ウイルス(AAV)ベクターが患者さんの視力や聴力回復に成功する様子を目の当たりに、私たちは「可能性」と「課題」の両面を見つけました —— ベクター生産の高コストと複雑さでした…

 

Determined to overcome these barriers, we built PackGene to revolutionize AAV manufacturing with innovative, scalable, and cost-effective solutions. Our work has enabled life-changing therapies, including a young boy born with congenital deafness. After receiving an AAV-based treatment produced by PackGene, he began responding to his family's voices. A few months later, he spoke his first word: “Dad.” His father wept with joy—a moment that reminded our team why we do what we do. It was more than just science; it was about restoring hope and giving families a future.

 

Today, PackGene is a global leader, serving clients in over 30 countries and partnering with more than 1,000 biopharmaceutical companies and research institutions. Our slogan, "Make Gene Therapy Affordable," reflects our unwavering mission. We focus on tackling key challenges in gene therapy development, including viral vector production and specific targeting, mRNA technologies, and GMP production at scale. We are committed to providing stable, qualified, cost-efficient, and fast services, along with technical support, to empower our gene therapy partners. Together, we aim to transform lives and build a healthier, better world.

さらに拡大
  • 1,000+

    クライアント

    生物製薬企業や研究機関から
  • 50,000+

    成功したプロジェクト

    研究からGMP生産への ワンストップソリューション
  • 120,000sqf

    GMP施設

    ウイルスベクター GMP 製造

ミッションと価値観

  • 紹介

    PackGene aims to Make Gene Therapy Affordable. We focus our work on several challenge areas within for rAAV based therapeutic pipeline including rAAV serotype selection, viral vector packaging, and GMP production at scale. We aim to provide stable, qualified, and cost-efficient fast services and technical support within these challenging areas with the overarching goal of helping our gene therapy partners make a better world.

  • ミッションステートメント

    Make Gene Therapy Affordable: To enhance gene therapy product development by providing an integrated one-stop shop solution to the gene therapy industry with high-quality products and services under world-class speed.

  • ビジョンステートメント

    Gene therapies are poised to revolutionize the world of medicine and address areas of unmet medical needs. PackGene’s proprietary π-Alpha 293 AAV High-yield Platform is positioned to alleviate industry-wide productivity bottlenecks while maintaining product safety.

    PackGene strives to deliver the most efficient gene therapy manufacturing platform, making novel gene therapies accessible and more affordable to patients in need.

  • 核心価値

    • Integrity: We do what we say and say what we do.
    • Innovation: Continuously improve our process to bring better therapies to the patients.
    • Patient First: We always put patients first in our day-to-day operations.
    • Customer dedication: We strive to exceed customers’ expectations in everyday work.
    • World-class delivery speed: It’s part of our genome to always provide world-class turnaround times because patients are waiting.
  • 紹介
  • ミッションステートメント
  • ビジョンステートメント
  • 核心価値

投資家関係

PackGene stands at the forefront as a global leader CRO and CDMO

Established in Massachusetts, USA, PackGene is currently expanding its capabilities with the construction of a GMP facility in Houston, Texas. The company provides a comprehensive range of services, including the production of rAAV-based GMP grade gene therapeutics, rAAV packaging, lentivirus packaging, mRNA, LNP, plasmid, and vector cloning. These initiatives have garnered widespread international collaboration and financial backing.

お問い合わせ

パートナーシップ

  • 国立精神・神経医療研究センター

  • 国立国際医療研究センター

  • 北里大学

販売代理店募集

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